Adam en Eva en andere verhalen over genetica / David & Jean-Jacques Cassiman ; [eindred. Philippe Degryse ; tek. Bert]Clinical relevance and patients relevance of delayed-release cysteamine bitartrate for patients with nephropathic cystinosis : clinical and patient/caregiver perspective / clinical perspective David Cassiman, Marlies Cornelissen, Mirian Janssen, Elena Levtchenko ; patient/caregiver perspective Marjolein Bos, Katrine Boullart, Fons Sondag